• |
  • |
  • |
  • |
Donate

Project

SPIES-006

Center:
Fiscal Year:
2024
Contact Information:
Project Description:
Title: SPIES-006: An intermediate size expanded access protocol of Elamipretide for subcutaneous injection in patients with genetically confirmed rare diseases with known mitochondrial dysfunction Role: Site PI Funding: Stealth BioTherapeutics November 2019-present Summary: This study is an open-label expanded access project treating patients with mitochondrial disease (MEGDEL, SANDO, NARP, MELAS).
Keyword(s):
Core Function(s):
Performing Research or Evaluation, Continuing Education/Community Training
Area of Emphasis
Other
Target Audience:
Children/Adolescents with Disabilities/SHCN
Unserved or Under-served Populations:
Other
Primary Target Audience Geographic Descriptor:
National
Funding Source:
COVID-19 Related Data:
N/A