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AUCD’s Maternal and Child Health Engagement supports the Autism CARES Programs, including LEND and DBP Programs.

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AUCD’s Public Health Team works to create health promotion and public health efforts that include people with disabilities.

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Project

MOUNTAINSIDE (0367-CL-1201)

Center:

TX-LoneStar, LEND

Fiscal Year:

2024

Contact Information:

Mary Kay Koenig
[email protected]
713-500-7164

Project Description:

Title: MOUNTAINSIDE (0367-CL-1201): A randomized, double-blind, placebo-controlled adaptive phase 2/3 Study with open-label extension to assess the efficacy, safety and tolerability of ASP0367 in participants with primary mitochondrial myopathy Role: Site PI Funding: Astellas Pharma Inc. October 2021-present Summary: This is a randomized, double-blind, placebo-controlled, oral dose, adaptive phase 2/3 study with open-label extension to evaluate the efficacy, safety and tolerability of ASP0367 in participants with primary mitochondrial myopathy.

Keyword(s):

Core Function(s):

Performing Research or Evaluation, Continuing Education/Community Training

Area of Emphasis

Other

Target Audience:

Children/Adolescents with Disabilities/SHCN

Unserved or Under-served Populations:

Other

Primary Target Audience Geographic Descriptor:

National

Funding Source: