Leigh Syndrome Roadmap Project: A Leigh Syndrome Natural History Study
Project Description:
Title: Leigh Syndrome Roadmap Project: A Leigh Syndrome Natural History Study
Role: Collaborator (Site PI-Russo)
Funding: The Leigh Syndrome International Consortium
2022-present
Summary: This study follows Leigh patients and perform standardized assessments over time in an attempt to identify appropriate clinical trial outcome measures.
Core Function(s):
Other Direct/Model Services, Demonstration Services
Area of Emphasis
Education & Early Intervention, Health-Related Activities, Other
Target Audience:
Adults with Disabilities
Unserved or Under-served Populations:
Disadvantaged Circumstances, Other
Primary Target Audience Geographic Descriptor:
National
COVID-19 Related Data:
N/A